Pompe Disease Websites
Pompe disease: a rare neuromuscular disorder
Pompe disease is a rare neuromuscular disorder that varies in its age of onset, symptoms, and rate of progression
Canadian Association of Pompe
The Canadian Association of Pompe was established to help persons in Canada, and elsewhere, become familiar with Pompe disease, and to support persons with Pompe disease.
Adult Stem Cell Research
Featuring the latest stem cell research success stories. Also provides stem cell therapy and treatment information!
Adult Stem Cell Research
Featuring the latest stem cell research success stories. Also provides stem cell therapy and treatment information!
Comet Study | A Research Study On Pompe Disease
The purpose of this research study is to compare the safety and effectiveness of two enzyme replacement therapies (the investigational medication neoGAA and the currently approved therapy alglucosidase alfa) in patients with late-onset Pompe disease who have not tried prior treatment.
Pompe foundation | Indian Pompe Disease helpline
Pompe foundation is a Trust to help ease the burden of pompe patients and parents of Pompe.
RARE-e-CONNECT - RARE-e-CONNECT
Secure multidisciplinary collaboration and knowledge sharing on rare diseases. For Healthcare Professionals and patients within Cyprus and abroad, large repository of medical centres in Europe and other countries with verified expertise in rare disease groups and rare diseases, Patient life stories, Continuous Medical